NEWS
Shire Receives CHMP Positive Opinion for VPRIVâ„¢
28.06.10
Shire Receives CHMP Positive Opinion for VPRIVâ„¢ (velaglucerase alfa) for the Treatment of Type 1 Gaucher Disease in the European Union Shire plc (LSE: SHP, NAS ...more
28.06.10
Shire Receives CHMP Positive Opinion for VPRIVâ„¢ (velaglucerase alfa) for the Treatment of Type 1 Gaucher Disease in the European Union Shire plc (LSE: SHP, NAS ...more
Cerezyme Emergency Treatment Program (CETP)
11.05.10
This program has been set up for the benefit of patients with type I and III Gaucher disease at high-risk for the development of progressive disease or complicati ...more
11.05.10
This program has been set up for the benefit of patients with type I and III Gaucher disease at high-risk for the development of progressive disease or complicati ...more
Product Supply Update
22.04.10
Cerezyme Genzyme achieved its goal of building a small inventory buffer during the first quarter. The current shipping allocation of 50 perce ...more
22.04.10
Cerezyme Genzyme achieved its goal of building a small inventory buffer during the first quarter. The current shipping allocation of 50 perce ...more
HG Shire Announces FDA Approval for Type 1 Gaucher Disease
02.03.10
HG Shire Announces FDA Approval of VPRIVTM (velaglucerase alfa for injection) for the Treatment of Type 1 Gaucher Disease Click here to see full press release: Press Release
02.03.10
HG Shire Announces FDA Approval of VPRIVTM (velaglucerase alfa for injection) for the Treatment of Type 1 Gaucher Disease Click here to see full press release: Press Release
Latest Cerezyme Update
17.02.10
Latest Cerezyme Update - 17th February 2010: Due to several factors including to improve manufacturing quality systems and perform preventative maintenance and ...more
17.02.10
Latest Cerezyme Update - 17th February 2010: Due to several factors including to improve manufacturing quality systems and perform preventative maintenance and ...more
Recommendations for treating patients with Gaucher disease with emerging enzyme products
15.01.10
A letter to the editor of the Blood Cells, Molecules and Diseases was published on the 18th December 2009 from Professor Timothy Cox, University of Cambridge Depa ...more
15.01.10
A letter to the editor of the Blood Cells, Molecules and Diseases was published on the 18th December 2009 from Professor Timothy Cox, University of Cambridge Depa ...more
European Medicines Agency's COMP Adopts Positive Opinion for the Orphan Drug Designation for Protalix's taliglucerase alfa
13.01.10
Press Release Source: Protalix BioTherapeutics, Inc. On Wednesday January 13, 2010, 7:30 am CARMIEL, Israel, Jan. 13 /PRNewswire/ -- Protali ...more
13.01.10
Press Release Source: Protalix BioTherapeutics, Inc. On Wednesday January 13, 2010, 7:30 am CARMIEL, Israel, Jan. 13 /PRNewswire/ -- Protali ...more
Guidelines for the restart of imiglucerase in patients with Gaucher disease: Recommendations from the European Working Group on Gaucher disease
07.01.10
Blood Cells, Molecules, and Diseases - 18th December 2009: Guidelines for the restart of imiglucerase in patients with Gaucher disease: Recommendations from the E ...more
07.01.10
Blood Cells, Molecules, and Diseases - 18th December 2009: Guidelines for the restart of imiglucerase in patients with Gaucher disease: Recommendations from the E ...more
Protalix Completes NDA Submission for taliglucerase alfa for the Treatment of Gaucher Disease
09.12.09
Protalix Completes NDA Submission for taliglucerase alfa for the Treatment of Gaucher’s Disease CARMIEL, Israel--(BUSINESS WIRE)--Protalix Biotherapeutics, Inc. ...more
09.12.09
Protalix Completes NDA Submission for taliglucerase alfa for the Treatment of Gaucher’s Disease CARMIEL, Israel--(BUSINESS WIRE)--Protalix Biotherapeutics, Inc. ...more
Shire Submits European Marketing Authorization
25.11.09
Shire Submits European Marketing Authorization Application (MAA) for velaglucerase alfa for the Treatment of Type 1 Gaucher Disease Committee for Medicinal Produc ...more
25.11.09
Shire Submits European Marketing Authorization Application (MAA) for velaglucerase alfa for the Treatment of Type 1 Gaucher Disease Committee for Medicinal Produc ...more
Force Majeure: Therapeutic measures in response to restricted supply of imiglucerase (Cerezyme) for patients with Gaucher disease
07.10.09
“Blood Cells, Molecules and Diseases”. Based on the findings of the meeting of the EWGGD on Thursday 10th September in Bad Honnef, Germany, this paper includes ...more
07.10.09
“Blood Cells, Molecules and Diseases”. Based on the findings of the meeting of the EWGGD on Thursday 10th September in Bad Honnef, Germany, this paper includes ...more
Cerezyme Emergency Treatment Program
30.09.09
Dear Friends, I am writing to inform you of some very important developments in the management of the shortage of Cerezyme, which is so severely affecting Gauc ...more
30.09.09
Dear Friends, I am writing to inform you of some very important developments in the management of the shortage of Cerezyme, which is so severely affecting Gauc ...more
Cerezyme Supply Update
20.08.09
Dear Friends, I am writing to you, at what is a very difficult time for the global Gaucher community, to provide an update on the supply of Cerezyme and how the ...more
20.08.09
Dear Friends, I am writing to you, at what is a very difficult time for the global Gaucher community, to provide an update on the supply of Cerezyme and how the ...more
Shire files treatment protocol
09.07.09
Shire has filed a treatment protocol for velaglucerase alfa for Gaucher Disease Lexington, Massachusetts, US – July 6th, 2009 – Shire plc (LSE: SHP ...more
09.07.09
Shire has filed a treatment protocol for velaglucerase alfa for Gaucher Disease Lexington, Massachusetts, US – July 6th, 2009 – Shire plc (LSE: SHP ...more
Protalix Approached by the FDA
06.07.09
Protalix Approached by the FDA to Consider Submitting a Treatment Protocol for the Use of prGCD in Patients with Gaucher Disease Allowing Expanded Access to prGCD ...more
06.07.09
Protalix Approached by the FDA to Consider Submitting a Treatment Protocol for the Use of prGCD in Patients with Gaucher Disease Allowing Expanded Access to prGCD ...more
Cerezyme Supply
18.06.09
Genzyme Temporarily Interrupts Production at Allston Plant Genzyme announce temporary closure of Boston manufacturing plant : Read Genzyme press ...more
18.06.09
Genzyme Temporarily Interrupts Production at Allston Plant Genzyme announce temporary closure of Boston manufacturing plant : Read Genzyme press ...more
Small Grant for Type 2 Research
01.05.09
The Gauchers Association has awarded a small grant to The Royal Free Hospital, London to purchase a batch of viral vectors as part of their research in gene therapy in Type II Gaucher disease.
01.05.09
The Gauchers Association has awarded a small grant to The Royal Free Hospital, London to purchase a batch of viral vectors as part of their research in gene therapy in Type II Gaucher disease.
Protalix Switch over Trial
23.03.09
Protalix BioTherapeutics Announces First Patient Enrolled in Open-Label, Switchover Trial of prGCD for the Treatment of Gaucher Disease Protalix BioTherapeutics ...more
23.03.09
Protalix BioTherapeutics Announces First Patient Enrolled in Open-Label, Switchover Trial of prGCD for the Treatment of Gaucher Disease Protalix BioTherapeutics ...more
Addenbrookes Homecare
13.02.09
Addenbrookes is pleased to announce that it has awarded the contract for the provision of homecare for patients with Gaucher disease jointly to Careology an ...more
13.02.09
Addenbrookes is pleased to announce that it has awarded the contract for the provision of homecare for patients with Gaucher disease jointly to Careology an ...more
New Fundraising Packs
12.01.09
New fundraising packs – We are pleased to announce the availability of our brand-new fundraising packs. They are available free to all of our members and fr ...more
12.01.09
New fundraising packs – We are pleased to announce the availability of our brand-new fundraising packs. They are available free to all of our members and fr ...more
Recieve e-mail alerts.
12.01.09
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12.01.09
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New Gauchers News online
12.01.09
Gaucher News online – Our January 2009 newsletter is now available in three formats – hard copy, e-mail, or as a .pdf file. Choose your preferred opti ...more
12.01.09
Gaucher News online – Our January 2009 newsletter is now available in three formats – hard copy, e-mail, or as a .pdf file. Choose your preferred opti ...more