Gaucher Association Logo

Promoting awareness, pioneering research and providing support and information for those affected by Gaucher disease.


Telephone: 01453 549231

Cerdelga Update

17 September 2014

Following the Food and Drug Administration (FDA) approval of Cerdelga as an oral treatment for certain adult Gaucher disease type 1 patients in August, press reports suggest that Genzyme has set a price for the US patients at $310,250 a year, see press release:

In Europe, marketing applications for Cerdelga are under review by the European Medicines Agency (EMA) and other regulatory authority, a decision is expected at the end of 2014.